Cognitive Effects of the BET Protein Inhibitor Apabetalone: A Prespecified Montreal Cognitive Assessment Analysis Nested in the BETonMACE Randomized Controlled Trial
Document Type
Article
Publication Date
10-12-2021
Publication Title
Journal of Alzheimer's Disease
Volume
83
Issue
4
First page number:
1703
Last page number:
1715
Abstract
Background: Epigenetic changes may contribute importantly to cognitive decline in late life including Alzheimer's disease (AD) and vascular dementia (VaD). Bromodomain and extra-terminal (BET) proteins are epigenetic 'readers' that may distort normal gene expression and contribute to chronic disorders. Objective: To assess the effects of apabetalone, a small molecule BET protein inhibitor, on cognitive performance of patients 70 years or older participating in a randomized trial of patients at high risk for major cardiovascular events (MACE). Methods: The Montreal Cognitive Assessment (MoCA) was performed on all patients 70 years or older at the time of randomization. 464 participants were randomized to apabetalone or placebo in the cognition sub-study. In a prespecified analysis, participants were assigned to one of three groups: MoCA score≥26 (normal performance), MoCA score 25-22 (mild cognitive impairment), and MoCA score≤21 (dementia). Exposure to apabetalone was equivalent in the treatment groups in each MoCA-defined group. Results: Apabetalone was associated with an increased total MoCA score in participants with baseline MoCA score of≤21 (p = 0.02). There was no significant difference in change from baseline in the treatment groups with higher MoCA scores. In the cognition study, more patients randomized to apabetalone discontinued study drug for adverse effects (11.3% versus 7.9%). Conclusion: In this randomized controlled study, apabetalone was associated with improved cognition as measured by MoCA scores in those with baseline scores of 21 or less. BET protein inhibitors warrant further investigation for late life cognitive disorders.
Keywords
Alzheimer’s disease; Apabetalone; BET inhibitor; Clinical trial; Epigenetics; Montreal cognitive assessment
Disciplines
Clinical Trials | Cognitive Neuroscience | Pharmacology
Language
English
Rights
IN COPYRIGHT. For more information about this rights statement, please visit http://rightsstatements.org/vocab/InC/1.0/
Repository Citation
Cummings, J.,
Schwartz, G. G.,
Nicholls, S. J.,
Khan, A.,
Halliday, C.,
Toth, P. P.,
Sweeney, M.,
Johansson, J. O.,
Wong, N. C.,
Kulikowski, E.,
Kalantar-Zadeh, K.,
Lebioda, K.,
Ginsberg, H. N.,
Winblad, B.,
Zetterberg, H.,
Ray, K.
(2021).
Cognitive Effects of the BET Protein Inhibitor Apabetalone: A Prespecified Montreal Cognitive Assessment Analysis Nested in the BETonMACE Randomized Controlled Trial.
Journal of Alzheimer's Disease, 83(4),
1703-1715.
http://dx.doi.org/10.3233/JAD-210570